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Meeting report

First published 2022

Clinical Trial Readiness for Spinal Muscular Atrophy: Experience of an International Educational-Training Initiative

Eduardo F. Tizzano, Vanessa Christie-Brown, Giovanni Baranello [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2023

The Rare Diseases Clinical Research Network: a model for clinical trial readiness

Joanne M. Lumsden, Tiina K. Urv

Therapeutic Advances in Rare Disease

Retricted access

Research article

First published 2013-4

From ClinicalTrials.gov trial registry to an analysis-ready database of clinical trial results

M Soledad Cepeda, Victor Lobanov, Jesse A Berlin

Clinical Trials

Open access

Research article

First published 2022-5

“Ready for What?”: Timing and Speculation in Alzheimer’s Disease Drug Development

Natassia F. Brenman, Richard Milne

Science,Technology,& Human Values

Retricted access

Research article

First published 2025-09

Vineland-3 Growth Scale Values: Psychometric Properties for Clinical Trial Readiness in SCN2A

Aaron J. Kaat, Lindsey Evans, Amanda N. Nili [...]

Journal of Child and Adolescent Psychopharmacology

Open access

Research article

First published 2023

SELENON-Related Myopathy Across the Life Span,a Cross-Sectional Study for Preparing Trial Readiness

Karlijn Bouman, Jan T. Groothuis, Jonne Doorduin [...]

Journal of Neuromuscular Diseases

Open access

Review article

First published 2025

The therapeutic readiness of probiotics in major depressive disorder: A systematic review of randomised controlled trials

Dinyadarshini Johnson, Dinesh Sangarran Ramachandram, Jack Doorly [...]

Journal of Psychopharmacology

Retricted access

Research article

First published 1995-10

Progress Toward Readiness for International Trials: Conference Summary

Dale N. Lawrence, Rodney Hoff

AIDS Research and Human Retroviruses

Retricted access

Research article

First published 2026-3

Self-Efficacy and Readiness to Change Among Women with Recent Gestational Diabetes Engaging in a Web-Based Lifestyle Intervention: The Balance After Baby Intervention Trial

Cara E. Saxon, Ellen W. Seely, Kaitlyn B. Bertin [...]

American Journal of Lifestyle Medicine

Open access

Review article

First published 2025

Enhancing and leveraging principal investigator and patient advocacy group collaboration in rare disease clinical research-meeting report from the rare Diseases Clinical Research Network

Kristen Wheeden, Sheridan Meyers, Kristin Anthony [...]

Therapeutic Advances in Rare Disease

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