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Research article

First published 2011-5

Chemical and Mechanistic Toxicology Evaluation of Exon Skipping Phosphorodiamidate Morpholino Oligomers in mdx Mice

Peter Sazani, Kirk P. Van Ness, Doreen L. Weller [...]

International Journal of Toxicology

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Research article

First published 1996-12

Resistance of Morpholino Phosphorodiamidate Oligomers to Enzymatic Degradation

Robert M. Hudziak, Elisabeth Barofsky, Douglas F. Barofsky [...]

Nucleic Acid Therapeutics

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Research article

First published 2016-8-30

Toxicological Characterization of Exon Skipping Phosphorodiamidate Morpholino Oligomers (PMOs) in Non-human Primates

Michael P. Carver, Jay S. Charleston, Courtney Shanks [...]

Journal of Neuromuscular Diseases

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Research article

First published 2000-08

Intracellular Delivery Strategies for Antisense Phosphorodiamidate Morpholino Oligomers

Chandramallika Ghosh, Patrick L. Iversen

Nucleic Acid Therapeutics

Open access

Research article

First published 2013-02

Development of Novel Bioanalytical Methods to Determine the Effective Concentrations of Phosphorodiamidate Morpholino Oligomers in Tissues and Cells

Frederick J. Schnell, Stacy L. Crumley, Dan V. Mourich [...]

BioResearch Open Access

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Research article

First published 2012-10

Peptide Conjugated Phosphorodiamidate Morpholino Oligomers Increase Survival of Mice Challenged with Ames Bacillus anthracis

Rekha G. Panchal, Bruce L. Geller, Brett Mellbye [...]

Nucleic Acid Therapeutics

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Research article

First published 2011-5

Repeat-Dose Toxicology Evaluation in Cynomolgus Monkeys of AVI-4658,a Phosphorodiamidate Morpholino Oligomer (PMO) Drug for the Treatment of Duchenne Muscular Dystrophy

Peter Sazani, Kirk P. Van Ness, Doreen L. Weller [...]

International Journal of Toxicology

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Research article

First published 2025-10

In Vivo Phage Display for the Identification of Muscle Homing Peptides to Improve the Delivery of Phosphorodiamidate Morpholino Oligomers for Duchenne Muscular Dystrophy Therapy

Anne-Fleur E. Schneider, Christa L. Tanganyika-de Winter, Hailiang Mei [...]

Nucleic Acid Therapeutics

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Other

First published 2010-3

Safety Pharmacology and Genotoxicity Evaluation of AVI-4658

Peter Sazani, Doreen L. Weller, Stephen B. Shrewsbury

International Journal of Toxicology

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Research article

First published 2021-11-30

Effects of Chronic,Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy

Margaret E. Benny Klimek, Maria Candida Vila, Katie Edwards [...]

Journal of Neuromuscular Diseases

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