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Research article

First published 2016-8-30

Toxicological Characterization of Exon Skipping Phosphorodiamidate Morpholino Oligomers (PMOs) in Non-human Primates

Michael P. Carver, Jay S. Charleston, Courtney Shanks [...]

Journal of Neuromuscular Diseases

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Research article

First published 2021-11-30

Effects of Chronic,Maximal Phosphorodiamidate Morpholino Oligomer (PMO) Dosing on Muscle Function and Dystrophin Restoration in a Mouse Model of Duchenne Muscular Dystrophy

Margaret E. Benny Klimek, Maria Candida Vila, Katie Edwards [...]

Journal of Neuromuscular Diseases

Free access

Research article

First published 2011-5

Repeat-Dose Toxicology Evaluation in Cynomolgus Monkeys of AVI-4658,a Phosphorodiamidate Morpholino Oligomer (PMO) Drug for the Treatment of Duchenne Muscular Dystrophy

Peter Sazani, Kirk P. Van Ness, Doreen L. Weller [...]

International Journal of Toxicology

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Research article

First published 2019

Identification of a Novel Deep Intronic Mutation in CAPN3 Presenting a Promising Target for Therapeutic Splice Modulation

Ying Hu, Payam Mohassel, Sandra Donkervoort [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2013-02

Development of Novel Bioanalytical Methods to Determine the Effective Concentrations of Phosphorodiamidate Morpholino Oligomers in Tissues and Cells

Frederick J. Schnell, Stacy L. Crumley, Dan V. Mourich [...]

BioResearch Open Access

Retricted access

Research article

First published 2001-10

Inhibition of Vesivirus Infections in Mammalian Tissue Culture with Antisense Morpholino Oligomers

David A. Stein, Douglas E. Skilling, Patrick L. Iversen [...]

Nucleic Acid Therapeutics

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Other

First published 2010-3

Safety Pharmacology and Genotoxicity Evaluation of AVI-4658

Peter Sazani, Doreen L. Weller, Stephen B. Shrewsbury

International Journal of Toxicology

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Research article

First published 2014-05

Evaluation of Tris[2-(Acryloyloxy)Ethyl]Isocyanurate Cross-Linked Polyethylenimine as Antisense Morpholino Oligomer Delivery Vehicle in Cell Culture and Dystrophic mdx Mice

Mingxing Wang, Bo Wu, Jay D. Tucker [...]

Human Gene Therapy

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Research article

First published 2000-08

Intracellular Delivery Strategies for Antisense Phosphorodiamidate Morpholino Oligomers

Chandramallika Ghosh, Patrick L. Iversen

Nucleic Acid Therapeutics

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Research article

First published 2003-02

HIV Tat Peptide Enhances Cellular Delivery of Antisense Morpholino Oligomers

Hong M. Moulton, Michelle C. Hase, Kristen M. Smith [...]

Nucleic Acid Therapeutics

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