Sage Journals: Discover world-class research

Open access

Research article

First published 2014

Human Growth Hormone Increases SMN Expression and Survival in Severe Spinal Muscular Atrophy Mouse Model

Duncan MacKenzie, Fahad Shamim, Kevin Mongeon [...]

Journal of Neuromuscular Diseases

Retricted access

Research article

First published 2022-11

Survival Motor Neuron Enhances Pluripotent Gene Expression and Facilitates Cell Reprogramming

Wei-Fang Chang, Tzu-Ying Lin, Min Peng [...]

Stem Cells and Development

Free access

Brief report

First published 2020

Blood Flow to the Spleen is Altered in a Mouse Model of Spinal Muscular Atrophy

Marc-Olivier Deguise, Ariane Beauvais, Bernard L. Schneider [...]

Journal of Neuromuscular Diseases

Retricted access

Brief report

First published 2012-03

Decreasing Disease Severity in Symptomatic,Smn −/−;SMN2 +/+,Spinal Muscular Atrophy Mice Following scAAV9-SMN Delivery

Jacqueline J. Glascock, Erkan Y. Osman, Mary J. Wetz [...]

Human Gene Therapy

Open access

Research article

First published 2024-11

Peripheral defects precede neuromuscular pathology in the Smn 2B/− mouse model of spinal muscular atrophy

Aoife Reilly, Ariane Beauvais, Majd Al-Aarg [...]

Journal of Neuromuscular Diseases

Retricted access

Research article

First published 2014-07

Translational Fidelity of Intrathecal Delivery of Self-Complementary AAV9–Survival Motor Neuron 1 for Spinal Muscular Atrophy

Marco A. Passini, Jie Bu, Amy M. Richards [...]

Human Gene Therapy

Free access

Research article

First published 2017

Analysis of Azithromycin Monohydrate as a Single or a Combinatorial Therapy in a Mouse Model of Severe Spinal Muscular Atrophy

Erkan Y. Osman, Charles W. Washington, Madeline E. Simon [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2015-11

Drug-like analogues of the parasitic worm-derived immunomodulator ES-62 are therapeutic in the MRL/Lpr model of systemic lupus erythematosus

D T Rodgers, M A Pineda, C J Suckling [...]

Lupus

Open access

Research article

First published 2024-1

Adenophorae Radix Reduces Fibrosis in a Bleomycin-Induced Pulmonary Fibrosis Mouse Model

Eui-Joong Kim, Jiwon Park, Chang-Hwan Yu [...]

Natural Product Communications

Retricted access

Research article

First published 2013-03

A Novel Morpholino Oligomer Targeting ISS-N1 Improves Rescue of Severe Spinal Muscular Atrophy Transgenic Mice

Haiyan Zhou, Narinder Janghra, Chalermchai Mitrpant [...]

Human Gene Therapy

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