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Open access

Research article

First published 2026-5

Carpal tunnel syndrome in mucopolysaccharidosis type I: clinical,surgical and histopathological findings

Boudewijn AW van Binsbergen, Joris A van Dongen, Linda Vriend [...]

Journal of Hand Surgery (European Volume)

Free access

Research article

First published 2011-5

Histopathologic Changes of the Ear in Canine Models of Mucopolysaccharidosis Types I and VII

J. Hordeaux, J. Deniaud, I. Bemelmans [...]

Veterinary Pathology

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Research article

First published 1992-08

Correction of Mucopolysaccharidosis Type I Fibroblasts by Retroviral-Mediated Transfer of the Human α- l -Iduronidase Gene

D. S. Anson, J. Bielicki, J. J. Hopwood

Human Gene Therapy

Open access

Research article

First published 2025-10

Ultrasonographic hip morphology in mucopolysaccharidosis type I Hurler after hematopoietic stem cell gene therapy

Maurizio De Pellegrin, Chiara Filisetti, Matilde Cossutta [...]

Journal of Children's Orthopaedics

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Research article

First published 2005-01

Gene Therapy for a Mucopolysaccharidosis Type I Murine Model with Lentiviral-IDUA Vector

Carmela Di Domenico, Guglielmo R.D. Villani, Daniele Di Napoli [...]

Human Gene Therapy

Open access

Research article

First published 2015-6

Characterization of knee alignment in children with mucopolysaccharidosis types I and II and outcome of treatment with guided growth

Elizabeth Ashby, Deborah Eastwood

Journal of Children's Orthopaedics

Free access

Research article

First published 2012-7

Intracerebroventricular Transplantation of Human Bone Marrow-Derived Multipotent Progenitor Cells in an Immunodeficient Mouse Model of Mucopolysaccharidosis Type I (MPS-I)

Zhenhong Nan, Laurie Shekels, Oleg Ryabinin [...]

Cell Transplantation

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Research article

First published 1999-09

Enzymatic Correction and Cross-Correction of Mucopolysaccharidosis Type I Fibroblasts by Adeno-Associated Virus-Mediated Transduction of the alpha-L-Iduronidase Gene

Seth D. Hartung, Rukmini G. Reddy, Chester B. Whitley [...]

Human Gene Therapy

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Research article

First published 2002-10

In Utero Injection of α -L-Iduronidase-Carrying Retrovirus in Canine Mucopolysaccharidosis Type I: Infection of Multiple Tissues and Neonatal Gene Expression

Lisa Meertens, Yongjun Zhao, Suzana Rosic-Kablar [...]

Human Gene Therapy

Free access

Research article

First published 2014-5

Biomarkers of bone remodeling in children with mucopolysaccharidosis types I,II,and VI

David A. Stevenson, Kyle Rudser, Alicia Kunin-Batson [...]

Journal of Pediatric Rehabilitation Medicine

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