Sage Journals: Discover world-class research

Open access

Brief report

First published 2021-07-30

Improving Care and Empowering Adults Living with SMA: A Call to Action in the New Treatment Era

Maggie C. Walter, Claudia Chiriboga, Tina Duong [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2019

Neurochemical markers in CSF of adolescent and adult SMA patients undergoing nusinersen treatment

Claudia D. Wurster, René Günther, Petra Steinacker [...]

Therapeutic Advances in Neurological Disorders

Free access

Research article

First published 2022-01-04

Neurofilament Levels in CSF and Serum in an Adult SMA Cohort Treated with Nusinersen

Kelly A. Rich, Ashley Fox, Mehmet Yalvac [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2021-07-30

Characterization of Adult Patients With SMA Treated in US Hospital Settings: A Natural History Study in the Premier Healthcare Database

Nicole B. Johnson, Crystal Proud, Christina L. Wassel [...]

Journal of Neuromuscular Diseases

Free access

Meeting report

First published 2020

Measuring Outcomes in Adults with Spinal Muscular Atrophy – Challenges and Future Directions – Meeting Report

V.A. Sansone, M.C. Walter, S. Attarian [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2019

Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational Study

Maggie C. Walter, Stephan Wenninger, Simone Thiele [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2018

Feasibility and safety of intrathecal treatment with nusinersen in adult patients with spinal muscular atrophy

Benjamin Stolte, Andreas Totzeck, Kathrin Kizina [...]

Therapeutic Advances in Neurological Disorders

Open access

Research article

First published 2025-9

Patient and caregiver spinal muscular atrophy treatment attribute preferences in Latin America

Victoria Saenz, Marijana Chlistalla, Nayara Carlos [...]

Journal of Neuromuscular Diseases

Free access

Research article

First published 2005-6

Temporal Expression of Alpha–Smooth Muscle Actin and Drebrin in Septal Interstitial Cells during Alveolar Maturation

Mie Yamada, Hidetake Kurihara, Katsuyuki Kinoshita [...]

Journal of Histochemistry & Cytochemistry

Free access

Brief report

First published 2016-8-30

What Matters Most: A Perspective From Adult Spinal Muscular Atrophy Patients

Michael Hunter, Chad Heatwole, Elizabeth Luebbe [...]

Journal of Neuromuscular Diseases

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