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Review article

First published 2013-04

Pre-existing Anti–Adeno-Associated Virus Antibodies as a Challenge in AAV Gene Therapy

Vedell Louis Jeune, Jakob A. Joergensen, Roger J. Hajjar [...]

Human Gene Therapy Methods (Part B)

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Research article

First published 1996-11

A Novel Adenovirus—Adeno-Associated Virus Hybrid Vector That Displays Efficient Rescue and Delivery of the AAV Genome

Krishna J. Fisher, W. Mark Kelley, John F. Burda [...]

Human Gene Therapy

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Research article

First published 2011-07

Safety of Liver Gene Transfer Following Peripheral Intravascular Delivery of Adeno-Associated Virus (AAV)-5 and AAV-6 in a Large Animal Model

Patricia Favaro, Jonathan D. Finn, Joshua I. Siner [...]

Human Gene Therapy

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Review article

First published 2026

Adeno-associated virus (AAV) mediated advanced therapeutic interventions for inherited and non-inherited cardiac disorders

Indu Singh, Anil Kumar, Awdhesh Kumar Chaudhary [...]

Journal of the Renin-Angiotensin-Aldosterone System

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Research article

First published 2024-12

Neuropathological Findings in Nonclinical Species Following Administration of Adeno-Associated Virus (AAV)-Based Gene Therapy Vectors

Brad Bolon, Elizabeth Buza, Elizabeth Galbreath [...]

Toxicologic Pathology

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Research article

First published 2006-04

Prevalence of Neutralizing Antibodies Against Adeno-Associated Virus (AAV) Types 2,5,and 6 in Cystic Fibrosis and Normal Populations: Implications for Gene Therapy Using AAV Vectors

Christine L. Halbert, A. Dusty Miller, Sharon Mcnamara [...]

Human Gene Therapy

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Research article

First published 2024-12

Pathology Findings and In-Life Correlates in the Nonclinical Development of Adeno-Associated Virus (AAV)-Based Retinal Gene Therapies

Helen S. Booler, Typhaine Lejeune, Oliver Turner [...]

Toxicologic Pathology

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Research article

First published 2018-12

Considerations for Preclinical Safety Assessment of Adeno-Associated Virus Gene Therapy Products

Basel T. Assaf, Laurence O. Whiteley

Toxicologic Pathology

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Research article

First published 2010-03

Optimized Adeno-Associated Virus (AAV)–Protein Phosphatase-5 Helper Viruses for Efficient Liver Transduction by Single-Stranded AAV Vectors: Therapeutic Expression of Factor IX at Reduced Vector Doses

Giridhara R. Jayandharan, Li Zhong, Brandon K. Sack [...]

Human Gene Therapy

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Research article

First published 2017-12

Differential Prevalence of Antibodies Against Adeno-Associated Virus in Healthy Children and Patients with Mucopolysaccharidosis III: Perspective for AAV-Mediated Gene Therapy

Haiyan Fu, Aaron S. Meadows, Ricardo J. Pineda [...]

Human Gene Therapy Clinical Development

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