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1-5 of 5 results for SMA3

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Free access

Research article

First published 2021-07-30

Effect of Discontinuation of Nusinersen Treatment in Long-Standing SMA3

Miriam Hiebeler, Angela Abicht, Peter Reilich [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2024-03-05

Treatment of Symptomatic Spinal Muscular Atrophy with Nusinersen: A Prospective Longitudinal Study on Scoliosis Progression

Hoi Ning Hayley Ip, Michael Kwan Leung Yu, Wilfred Hing Sang Wong [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2025-11

REGISTRE SMA FRANCE: A nationwide observational registry of patients with spinal muscular atrophy in France

Lamiae Grimaldi, Rocio Garcia-Uzquiano, Marta Gomez-Garcia de la Banda [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2025-11

Epidemiology of spinal muscular atrophy in Aotearoa-New Zealand

Richard H Roxburgh, Alana Cavadino, Miriam Rodrigues [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2019

Safety and Treatment Effects of Nusinersen in Longstanding Adult 5q-SMA Type 3 – A Prospective Observational Study

Maggie C. Walter, Stephan Wenninger, Simone Thiele [...]

Journal of Neuromuscular Diseases