Sage Journals: Discover world-class research

Retricted access

Review article

First published 2019-1

Nusinersen: A Treatment for Spinal Muscular Atrophy

Melanie K. Claborn, Debra L. Stevens, Cheri K. Walker [...]

Annals of Pharmacotherapy

Open access

Research article

First published 2023-1-3

Improvements in Walking Distance during Nusinersen Treatment – A Prospective 3-year SMArtCARE Registry Study

Astrid Pechmann, Max Behrens, Katharina Dörnbrack [...]

Journal of Neuromuscular Diseases

Open access

Case report

First published 2023-07-04

Symptomatic intracranial hypertension in an adult patient with spinal muscular atrophy and arachnoid cysts receiving nusinersen

Gerrit Machetanz, Marc Grziwotz, Luisa Semmler [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2024-03-05

Treatment of Symptomatic Spinal Muscular Atrophy with Nusinersen: A Prospective Longitudinal Study on Scoliosis Progression

Hoi Ning Hayley Ip, Michael Kwan Leung Yu, Wilfred Hing Sang Wong [...]

Journal of Neuromuscular Diseases

Open access

Review article

First published 2026-3

Real-world evidence on nusinersen treatment of persons with SMA: a focused review

Susan E Matesanz, Richard S Finkel

Journal of Neuromuscular Diseases

Open access

Research article

First published 2023-09-08

DEVOTE Study Exploring Higher Dose of Nusinersen in Spinal Muscular Atrophy: Study Design and Part A Results

Richard S. Finkel, John W. Day, Samuel Ignacio Pascual Pascual [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2020

Experiences from treating seven adult 5q spinal muscular atrophy patients with Nusinersen

Elisabeth Jochmann, Robert Steinbach, Thomas Jochmann [...]

Therapeutic Advances in Neurological Disorders

Open access

Research article

First published 2024-6

Nusinersen therapy changed the natural course of spinal muscular atrophy type 1: What about spine and hip?

Niyazi Erdem Yasar, Guzelali Ozdemir, Elif Uzun Ata [...]

Journal of Children's Orthopaedics

Free access

Research article

First published 2021-07-30

Effect of Discontinuation of Nusinersen Treatment in Long-Standing SMA3

Miriam Hiebeler, Angela Abicht, Peter Reilich [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2019

Neurochemical markers in CSF of adolescent and adult SMA patients undergoing nusinersen treatment

Claudia D. Wurster, René Günther, Petra Steinacker [...]

Therapeutic Advances in Neurological Disorders

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