Sage Journals: Discover world-class research

Retricted access

Research article

First published 2010-09

Antisense Modulation of Both Exonic and Intronic Splicing Motifs Induces Skipping of a DMD Pseudo-Exon Responsible for X-Linked Dilated Cardiomyopathy

Paola Rimessi, Marina Fabris, Matteo Bovolenta [...]

Human Gene Therapy

Open access

Meeting report

First published 2024-03-05

Draft Guidance for Industry Duchenne Muscular Dystrophy,Becker Muscular Dystrophy,and Related Dystrophinopathies – Developing Potential Treatments for the Entire Spectrum of Disease

Craig McDonald, Eric Camino, Rafael Escandon [...]

Journal of Neuromuscular Diseases

Open access

Review article

First published 2023

Cardiac therapies for Duchenne muscular dystrophy

Md Nur Ahad Shah, Toshifumi Yokota

Therapeutic Advances in Neurological Disorders

Open access

Review article

First published 2017

Cardiac Involvement Classification and Therapeutic Management in Patients with Duchenne Muscular Dystrophy

Abdallah Fayssoil, Soumeth Abasse, Katy Silverston

Journal of Neuromuscular Diseases

Retricted access

Brief report

First published 2008-08

Adeno-Associated Virus Serotype-9 Microdystrophin Gene Therapy Ameliorates Electrocardiographic Abnormalities in mdx Mice

Brian Bostick, Yongping Yue, Yi Lai [...]

Human Gene Therapy

Free access

Research article

First published 2014-5

Cardiac Management of Ventilator-Assisted Individuals with Duchenne Muscular Dystrophy

Lauren O’Brien, Robert Varadi, Roger S Goldstein [...]

Chronic Respiratory Disease

Free access

Research article

First published 2017

Progression of Duchenne Cardiomyopathy Presenting with Chest Pain and Troponin Elevation

Kan N. Hor, Pace Johnston, Kathi Kinnett [...]

Journal of Neuromuscular Diseases

Open access

Case report

First published 2018

Mechanical thrombectomy in a young stroke patient with Duchenne muscular dystrophy

Charlotte Spicher, Ruth Schneider, Peter Mönnings [...]

Therapeutic Advances in Neurological Disorders

Open access

Research article

First published 2024-12

Long-Term Survival and Myocardial Function Following Systemic Delivery of Delandistrogene Moxeparvovec in DMD MDX Rats

Stephen Baine, Chris Wier, Luke Lemmerman [...]

Human Gene Therapy

Open access

Research article

First published 2022

Characterizing the Occurrence of Key Clinical Milestones in Duchenne Muscular Dystrophy in the United States Using Real-World Data

Shelagh M. Szabo, Alexa C. Klimchak, Christina Qian [...]

Journal of Neuromuscular Diseases

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