Sage Journals: Discover world-class research

Open access

Research article

First published 2023

Evaluation of rAAVrh74 gene therapy vector seroprevalence by measurement of total binding antibodies in patients with Duchenne muscular dystrophy

Natalie L. Goedeker, Sachi D. Dharia, Danielle A. Griffin [...]

Therapeutic Advances in Neurological Disorders

Open access

Research article

First published 2021-04

Rachael A. Potter, Danielle A. Griffin, Kristin N. Heller [...]

Human Gene Therapy

Retricted access

Research article

First published 2017-09

Deborah A. Zygmunt, Kelly E. Crowe, Kevin M. Flanigan [...]

Human Gene Therapy

Open access

Research article

First published 2022-01-04

Stella Mitrani-Rosenbaum, Lena Yakovlev, Michal Becker Cohen [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2023-09-08

Deborah A. Zygmunt, Patricia Lam, Anna Ashbrook [...]

Journal of Neuromuscular Diseases

Retricted access

Research article

First published 2017-06

Megan L. Cramer, Guohong Shao, Louise R. Rodino-Klapac [...]

Human Gene Therapy