Sage Journals: Discover world-class research

Retricted access

Research article

First published 2019-9

Evaluating Prognostic Factors for Liver Transplantation Among United States Patients With Hereditary Transthyretin-Mediated (hATTR) Amyloidosis Using National Registry Data

Danielle Brandman, Hollis Lin, Anastasia McManus [...]

Progress in Transplantation

Free access

Case report

First published 2020

Familial Oculo-Leptomeningeal Transthyretin Amyloidosis Caused by Leu55Arg Mutation

Felix Kleefeld, Fabian Knebel, Dennis Eurich [...]

Journal of Neuromuscular Diseases

Retricted access

Research article

First published 2022-1

Pupillometry: An objective test to assess endocular hereditary transthyretin amyloidosis

João Heitor Marques, Luísa Malheiro, Jorge Malheiro [...]

European Journal of Ophthalmology

Open access

Research article

First published 2020-06

Population Pharmacokinetic–Pharmacodynamic Modeling of Inotersen,an Antisense Oligonucleotide for Treatment of Patients with Hereditary Transthyretin Amyloidosis

Rosie Z. Yu, Jon W. Collins, Shannon Hall [...]

Nucleic Acid Therapeutics

Open access

Case report

First published 2024

Patisiran exposure in early pregnancy: a case report

Valentin Loser, Thomas Baumgartner, Hélène Legardeur [...]

Therapeutic Advances in Neurological Disorders

Open access

Review article

First published 2025

Neurological efficacy and safety of RNA therapeutics in hereditary transthyretin amyloidosis: a systematic review and meta-analysis of randomized controlled trials

Maha Sajjad, Rabia Ashraf, Riya Bhagwan [...]

Therapeutic Advances in Cardiovascular Disease

Retricted access

Research article

First published 2020-04

Underlying Immune Disorder May Predispose Some Transthyretin Amyloidosis Subjects to Inotersen-Mediated Thrombocytopenia

Padmakumar Narayanan, Brian R. Curtis, Lijiang Shen [...]

Nucleic Acid Therapeutics

Search results

Evaluating Prognostic Factors for Liver Transplantation Among United States Patients With Hereditary Transthyretin-Mediated (hATTR) Amyloidosis Using National Registry Data

Familial Oculo-Leptomeningeal Transthyretin Amyloidosis Caused by Leu55Arg Mutation

Pupillometry: An objective test to assess endocular hereditary transthyretin amyloidosis

Population Pharmacokinetic–Pharmacodynamic Modeling of Inotersen,an Antisense Oligonucleotide for Treatment of Patients with Hereditary Transthyretin Amyloidosis

Patisiran exposure in early pregnancy: a case report

Neurological efficacy and safety of RNA therapeutics in hereditary transthyretin amyloidosis: a systematic review and meta-analysis of randomized controlled trials

Underlying Immune Disorder May Predispose Some Transthyretin Amyloidosis Subjects to Inotersen-Mediated Thrombocytopenia