Sage Journals: Discover world-class research

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Research article

First published 2012-10

Intrablastocyst injection with human CD34 + /CD133 + cells increase survival of immunocompetent fumarylacetoacetate hydrolase knockout mice

Emanuele Marra, Paolo Turrini, Marco Tripodi [...]

Laboratory Animals

Open access

Research article

First published 2019-1

Autologous Gene and Cell Therapy Provides Safe and Long-Term Curative Therapy in A Large Pig Model of Hereditary Tyrosinemia Type 1

Raymond D. Hickey, Clara T. Nicolas, Kari Allen [...]

Cell Transplantation

Retricted access

Research article

First published 1997-03

Adenovirus-Mediated Gene Therapy in a Mouse Model of Hereditary Tyrosinemia Type I

Ken Overturf, Muhsen Al-Dhalimy, Ching Nan Ou [...]

Human Gene Therapy

Open access

Research article

First published 2018

Girl With Tyrosinemia Type 1 and Executive Dysfunctions Treated With Methylphenidate

Annik Simons, Francois Eyskens, Elien Raets [...]

Journal of Inborn Errors of Metabolism and Screening

Retricted access

Research article

First published 2019-04

Efficient Generation of an Fah/Rag2 Dual-Gene Knockout Porcine Cell Line Using CRISPR/Cas9 and Adenovirus

Mengyu Gao, Bingqi Zhang, Yuting He [...]

DNA and Cell Biology

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Research article

First published 1998-02

Ex Vivo Hepatic Gene Therapy of a Mouse Model of Hereditary Tyrosinemia Type I

Ken Overturf, Muhsen Al-Dhalimy, Kara Manning [...]

Human Gene Therapy

Retricted access

Research article

First published 2021-03

Induced Liver Regeneration Enhances CRISPR/Cas9-Mediated Gene Repair in Tyrosinemia Type 1

Qing-Shuo Zhang, Amita Tiyaboonchai, Sean Nygaard [...]

Human Gene Therapy

Retricted access

Research article

First published 2019-06

Hepatotoxicity and Toxicology of In Vivo Lentiviral Vector Administration in Healthy and Liver-Injury Mouse Models

Robert Allen Kaiser, Clara Teresa Nicolas, Kari Lynn Allen [...]

Human Gene Therapy Clinical Development

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Research article

First published 2009-10

Fine Specificity of Autoantibodies Induced By Mouse Hepatitis Virus A59

Maite Duhalde-Vega, José Luis Aparicio, Lilia A. Retegui

Viral Immunology

Free access

Research article

First published 2021-12

Low-Frequency Vibration Promotes Tumor Necrosis Factor-α Production to Increase Cartilage Degeneration in Knee Osteoarthritis

Peng-Ming Yu, Yang Lin, Chi Zhang [...]

CARTILAGE

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