Sage Journals: Discover world-class research

Retricted access

Research article

First published 2026-3

Brain-Directed AAV Gene Therapy Rescues a Mouse Model of the CLN5 Form of Neuronal Ceroid Lipofuscinosis Disease and Normalizes a Blood Plasma Biomarker of Neurodegeneration

Wenfei Liu, Amy F. Geard, Giulia Massaro [...]

Human Gene Therapy

Retricted access

Research article

First published 2014-03

Treatment of Congenital Neurotransmitter Deficiencies by Intracerebral Ventricular Injection of an Adeno-Associated Virus Serotype 9 Vector

Ni-Chung Lee, Yin-Hsiu Chien, Min-Hsiu Hu [...]

Human Gene Therapy

Retricted access

Research article

First published 1993-02

Gene Therapy for the Treatment of Brain Tumors Using Intra-Tumoral Transduction with the Thymidine Kinase Gene and Intravenous Ganciclovir. National Institutes of Health

Edward H. Oldfield, Zvi Ram, Kenneth W. Culver [...]

Human Gene Therapy

Retricted access

Research article

First published 1994-03

Gene Therapy for the Treatment of Malignant Brain Tumors with In Vivo Tumor Transduction with the Herpes Simplex Thymidine Kinase Gene/Ganciclovir System. Iowa Methodist Medical Center,Des Moines,Iowa

Kenneth W. Culver, John Van Gilder, Charles J. Link [...]

Human Gene Therapy

Retricted access

Research article

First published 1994-07

Gene Therapy for the Treatment of Recurrent Pediatric Malignant Astrocytomas with In Vivo Tumor Transduction with the Herpes Simplex Thymidine Kinase Gene/Ganciclovir System. Childrens Hospital,Los Angeles,California

Corey Raffel, Kenneth Culver, Donald Kohn [...]

Human Gene Therapy

Retricted access

Review article

First published 1999-07

Review : Gene Expression after Cerebral Ischemia

Sean I. Savitz, Daniel M. Rosenbaum

The Neuroscientist

Open access

Research article

First published 2026-3

Systemic Administration of AAV9-G266A with Focused Ultrasound Enables Robust Brain Transduction with Minimal Liver Transduction

Andrew T. Nelson, Aidan Smith, Colleen T. Curley [...]

Human Gene Therapy

Open access

Review article

First published 2021

Growth Factor Therapy for Parkinson’s Disease: Alternative Delivery Systems

Sarah Jarrin, Abrar Hakami, Ben Newland [...]

Journal of Parkinson’s Disease

Retricted access

Research article

First published 2007-11

Efficient Gene Transfer via Retrograde Transport in Rodent and Primate Brains Using a Human Immunodeficiency Virus Type 1-Based Vector Pseudotyped with Rabies Virus Glycoprotein

Shigeki Kato, Ken-Ichi Inoue, Kenta Kobayashi [...]

Human Gene Therapy

Retricted access

Research article

First published 2017-02

Distribution and Penetration of Intracerebroventricularly Administered 2′OMePS Oligonucleotide in the Mouse Brain

João Casaca-Carreira, Yasin Temel, Iñaki Larrakoetxea [...]

Nucleic Acid Therapeutics

Search results