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1-4 of 4 results for pantothenate kinase-associated neurodegeneration treatment

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Open access

Research article

First published 2019-8

The FOsmetpantotenate Replacement Therapy (FORT) randomized,double-blind,Placebo-controlled pivotal trial: Study design and development methodology of a novel primary efficacy outcome in patients with pantothenate kinase-associated neurodegeneration

Thomas Klopstock, Maria L Escolar, Randall D Marshall [...]

Clinical Trials

Open access

Case report

First published 2024

Henry-Marcelo Rodriguez-Perez, Olga-Berenice Reyes-Flores, Yazmin Quiñonez-Pacheco [...]

Sage Open Medical Case Reports

Retricted access

Research article

First published 2020-3

Jenny L. Wilson, Allison Gregory, Katrina Wakeman [...]

Journal of Child Neurology

Open access

Article commentary

First published 2019

Suzanne Jackowski

Neuroscience Insights