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Research article

First published 2000-9

Phenotype Correction in Murine Mucopolysaccharidosis Type VII by Transplantation of Human Amniotic Epithelial Cells after Adenovirus-Mediated Gene Transfer

Motomichi Kosuga, Satori Takahashi, Kyoko Sasaki [...]

Cell Transplantation

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Research article

First published 2011-5

Histopathologic Changes of the Ear in Canine Models of Mucopolysaccharidosis Types I and VII

J. Hordeaux, J. Deniaud, I. Bemelmans [...]

Veterinary Pathology

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Research article

First published 2005-7

Early Onset of Lysosomal Storage Disease in a Murine Model of Mucopolysaccharidosis Type VII: Undegraded Substrate Accumulates in Many Tissues in the Fetus and Very Young MPS VII Mouse

Carole Vogler, Beth Levy, Nancy Galvin [...]

Pediatric and Developmental Pathology

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Research article

First published 2014-03

Central Nervous System Delivery of Helper-Dependent Canine Adenovirus Corrects Neuropathology and Behavior in Mucopolysaccharidosis Type VII Mice

Lorena Ariza, Lydia Giménez-Llort, Aurélie Cubizolle [...]

Human Gene Therapy

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Research article

First published 2000-03

Recombinant Adeno-Associated Virus-Mediated Correction of Lysosomal Storage within the Central Nervous System of the Adult Mucopolysaccharidosis Type VII Mouse

Thomas J. Sferra, Guang Qu, David McNeely [...]

Human Gene Therapy

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Research article

First published 2000-05

Reversal of Pathology in the Entire Brain of Mucopolysaccharidosis Type VII Mice after Lentivirus-Mediated Gene Transfer

Assumpció Bosch, Emmanuelle Perret, Nathalie Desmaris [...]

Human Gene Therapy

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Research article

First published 1999-01

Neonatal Intramuscular Injection with Recombinant Adeno-Associated Virus Results in Prolonged beta-Glucuronidase Expression in Situ and Correction of Liver Pathology in Mucopolysaccharidosis Type VII Mice

Thomas M. Daly, Torayuki Okuyama, Carole Vogler [...]

Human Gene Therapy

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Research article

First published 1991-07

Correction of Murine Mucopolysaccharidosis Type VII (MPS VII) by Bone Marrow Transplantation and Gene Transfer Therapy

Edward H. Birkenmeier

Human Gene Therapy

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Research article

First published 2014-09

Lentiviral-Mediated Gene Therapy Results in Sustained Expression of β-Glucuronidase for up to 12 Months in the Gus mps/mps and up to 18 Months in the Gus tm(L175F)Sly Mouse Models of Mucopolysaccharidosis Type VII

Ainslie L.K. Derrick-Roberts, Carmen E. Pyragius, Xenia M. Kaidonis [...]

Human Gene Therapy

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Research article

First published 2001-5

Widespread Distribution of Adenovirus-Transduced Monkey Amniotic Epithelial Cells after Local Intracerebral Injection: Implication for Cell-Mediated Therapy for Lysosome Storage Disorders

Motomichi Kosuga, Satoru Takahashi, Akiko Tanabe [...]

Cell Transplantation

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