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Research article

First published 2021-11-30

Interrogation of Dystrophin and Dystroglycan Complex Protein Turnover After Exon Skipping Therapy

James S. Novak, Rita Spathis, Utkarsh J. Dang [...]

Journal of Neuromuscular Diseases

Retricted access

Research article

First published 2018-03

Dual AAV Gene Therapy for Duchenne Muscular Dystrophy with a 7-kb Mini-Dystrophin Gene in the Canine Model

Kasun Kodippili, Chady H. Hakim, Xiufang Pan [...]

Human Gene Therapy

Retricted access

Research article

First published 2015-10

Human α7 Integrin Gene ( ITGA7 ) Delivered by Adeno-Associated Virus Extends Survival of Severely Affected Dystrophin/Utrophin-Deficient Mice

Kristin N. Heller, Chrystal L. Montgomery, Kimberly M. Shontz [...]

Human Gene Therapy

Free access

Research article

First published 2008-8

Cardiac involvement in the dystrophinopathies

Mark W. Russell, DeWayne Townsend, Joseph M. Metzger

Journal of Pediatric Rehabilitation Medicine

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Research article

First published 2001-01

Muscle-Specific Promoters May Be Necessary for Adeno-Associated Virus-Mediated Gene Transfer in the Treatment of Muscular Dystrophies

Laurence Cordier, Guang-Ping Gao, Andrew A. Hack [...]

Human Gene Therapy

Free access

Research article

First published 2016

N-terminal α Dystroglycan (αDG-N): A Potential Serum Biomarker for Duchenne Muscular Dystrophy

Kelly E. Crowe, Guohong Shao, Kevin M. Flanigan [...]

Journal of Neuromuscular Diseases

Retricted access

Research article

First published 2017-3

GWAS Identifies New Loci for Painful Temporomandibular Disorder: Hispanic Community Health Study/Study of Latinos

A.E. Sanders, D. Jain, T. Sofer [...]

Journal of Dental Research

Open access

Research article

First published 2021-04

Preclinical Systemic Delivery of Adeno-Associated α-Sarcoglycan Gene Transfer for Limb-Girdle Muscular Dystrophy

Danielle A. Griffin, Eric R. Pozsgai, Kristin N. Heller [...]

Human Gene Therapy

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