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Research article

First published 2018-04

Slow Infusion of Recombinant Adeno-Associated Viruses into the Mouse Cerebrospinal Fluid Space

Dan Wang, Jia Li, Karen Tran [...]

Human Gene Therapy Methods (Part B)

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Research article

First published 2021-12

Isolating Natural Adeno-Associated Viruses from Primate Tissues with a High-Fidelity Polymerase

Qiang Wang, Kalyani Nambiar, James M. Wilson

Human Gene Therapy

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Research article

First published 2017-06

A Scalable and Accurate Method for Quantifying Vector Genomes of Recombinant Adeno-Associated Viruses in Crude Lysate

Jianzhong Ai, Raed Ibraheim, Phillip W.L. Tai [...]

Human Gene Therapy Methods (Part B)

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Research article

First published 2022-11

Characterizing Complex Populations of Endogenous Adeno-Associated Viruses by Single-Genome Amplification

Kalyani Nambiar, Qiang Wang, Hanying Yan [...]

Human Gene Therapy

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Research article

First published 2010-03

Optimized Adeno-Associated Virus (AAV)–Protein Phosphatase-5 Helper Viruses for Efficient Liver Transduction by Single-Stranded AAV Vectors: Therapeutic Expression of Factor IX at Reduced Vector Doses

Giridhara R. Jayandharan, Li Zhong, Brandon K. Sack [...]

Human Gene Therapy

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Research article

First published 2022-04

Human and Insect Cell-Produced Recombinant Adeno-Associated Viruses Show Differences in Genome Heterogeneity

Ngoc Tam Tran, Emilie Lecomte, Sylvie Saleun [...]

Human Gene Therapy

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News

First published 2021-12

Membranous Bubbles: High-Purity and High-Titer Exosomes as the Potential Solution for Adeno-Associated Viruses to Evade Neutralization?

Manish Muhuri, Guangping Gao

Human Gene Therapy

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Research article

First published 1999-04

Highly Purified Recombinant Adeno-Associated Virus Vectors Are Biologically Active and Free of Detectable Helper and Wild-Type Viruses

K. Reed Clark, Xinglou Liu, John P. Mcgrath [...]

Human Gene Therapy

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Editorial

First published 2023-11

Integration of Gene Therapy Vectors: A Risk Factor for Tumorigenesis or Another Commensal Property of Adeno-Associated Viruses That Benefits Long-Term Transgene Expression?

Phillip W.L. Tai

Human Gene Therapy

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Research article

First published 2021-09-14

Electrostatic Coating of Viral Particles for Gene Delivery Applications in Muscular Dystrophies: Influence of Size on Stability and Antibody Protection

Marta Guerra-Rebollo, María Stampa, Miguel Ángel Lázaro [...]

Journal of Neuromuscular Diseases

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