Search results: Sage Journals

Free accessAbstractFirst published June, 1990

Tissue and cellular distribution of alpha-L-iduronidase in the pig.

H Sakuda, A Kusaba, T Ohshita [...]

Journal of Histochemistry & Cytochemistry

Restricted accessResearch articleFirst published August, 1996

Myoblast Gene Therapy in Canine Mucopolysaccharidosis I: Abrogation by an Immune Response to α - l -Iduronidase

Robert M. Shull, Xiaochen Lu, Michael F. McEntee [...]

Human Gene Therapy

Restricted accessResearch articleFirst published September, 1995

In Vivo Delivery of Human α - l -Iduronidase in Mice Implanted with Neo-Organs

Anna Salvetti, Philippe Moullier, Véronique Cornet [...]

Human Gene Therapy

Restricted accessResearch articleFirst published August, 1992

Correction of Mucopolysaccharidosis Type I Fibroblasts by Retroviral-Mediated Transfer of the Human α- l -Iduronidase Gene

D. S. Anson, J. Bielicki, J. J. Hopwood

Human Gene Therapy

Restricted accessResearch articleFirst published June, 1999

Gene Therapy for Canine alpha-L-Iduronidase Deficiency: In Utero Adoptive Transfer of Genetically Corrected Hematopoietic Progenitors Results in Engraftment but Not Amelioration of Disease

Carolyn Lutzko, Fusayuki Omori, Anthony C. G. Abrams-Ogg [...]

Human Gene Therapy

Restricted accessCase reportFirst published May, 2017

Role of rehabilitation in Hurler's syndrome

Sudhir Ramkishore Mishra, Mona Shastri, Jaishree Ramesh

Journal of Back and Musculoskeletal Rehabilitation

Restricted accessResearch articleFirst published December, 2009

Mutational Analysis of the α-L-Iduronidase Gene in Three Egyptian Families: Identification of Three Novel Mutations and Five Novel Polymorphisms

Khalda Amr, Ahmed Katoury, Mohamed Abdel-Hamid [...]

Genetic Testing and Molecular Biomarkers

Restricted accessResearch articleFirst published October, 2002

In Utero Injection of α -L-Iduronidase-Carrying Retrovirus in Canine Mucopolysaccharidosis Type I: Infection of Multiple Tissues and Neonatal Gene Expression

Lisa Meertens, Yongjun Zhao, Suzana Rosic-Kablar [...]

Human Gene Therapy

Restricted accessResearch articleFirst published September, 1999

Enzymatic Correction and Cross-Correction of Mucopolysaccharidosis Type I Fibroblasts by Adeno-Associated Virus-Mediated Transduction of the alpha-L-Iduronidase Gene

Seth D. Hartung, Rukmini G. Reddy, Chester B. Whitley [...]

Human Gene Therapy

Restricted accessResearch articleFirst published November, 2006

Limited Transgene Immune Response and Long-Term Expression of Human α -L-Iduronidase in Young Adult Mice with Mucopolysaccharidosis Type I by Liver-Directed Gene Therapy

C. Di Domenico, D. Di Napoli, E. Gonzalez Y Reyero [...]

Human Gene Therapy

Free accessAbstractFirst published June, 1990

Tissue and cellular distribution of alpha-L-iduronidase in the pig.

H Sakuda, A Kusaba, T Ohshita [...]

Journal of Histochemistry & Cytochemistry

Restricted accessResearch articleFirst published August, 1996

Myoblast Gene Therapy in Canine Mucopolysaccharidosis I: Abrogation by an Immune Response to α - l -Iduronidase

Robert M. Shull, Xiaochen Lu, Michael F. McEntee [...]

Human Gene Therapy

Restricted accessResearch articleFirst published September, 1995

In Vivo Delivery of Human α - l -Iduronidase in Mice Implanted with Neo-Organs

Anna Salvetti, Philippe Moullier, Véronique Cornet [...]

Human Gene Therapy

Restricted accessResearch articleFirst published August, 1992

Correction of Mucopolysaccharidosis Type I Fibroblasts by Retroviral-Mediated Transfer of the Human α- l -Iduronidase Gene

D. S. Anson, J. Bielicki, J. J. Hopwood

Human Gene Therapy

Restricted accessResearch articleFirst published June, 1999

Gene Therapy for Canine alpha-L-Iduronidase Deficiency: In Utero Adoptive Transfer of Genetically Corrected Hematopoietic Progenitors Results in Engraftment but Not Amelioration of Disease

Carolyn Lutzko, Fusayuki Omori, Anthony C. G. Abrams-Ogg [...]

Human Gene Therapy

Restricted accessCase reportFirst published May, 2017

Role of rehabilitation in Hurler's syndrome

Sudhir Ramkishore Mishra, Mona Shastri, Jaishree Ramesh

Journal of Back and Musculoskeletal Rehabilitation

Restricted accessResearch articleFirst published December, 2009

Mutational Analysis of the α-L-Iduronidase Gene in Three Egyptian Families: Identification of Three Novel Mutations and Five Novel Polymorphisms

Khalda Amr, Ahmed Katoury, Mohamed Abdel-Hamid [...]

Genetic Testing and Molecular Biomarkers

Restricted accessResearch articleFirst published October, 2002

In Utero Injection of α -L-Iduronidase-Carrying Retrovirus in Canine Mucopolysaccharidosis Type I: Infection of Multiple Tissues and Neonatal Gene Expression

Lisa Meertens, Yongjun Zhao, Suzana Rosic-Kablar [...]

Human Gene Therapy

Restricted accessResearch articleFirst published September, 1999

Enzymatic Correction and Cross-Correction of Mucopolysaccharidosis Type I Fibroblasts by Adeno-Associated Virus-Mediated Transduction of the alpha-L-Iduronidase Gene

Seth D. Hartung, Rukmini G. Reddy, Chester B. Whitley [...]

Human Gene Therapy

Restricted accessResearch articleFirst published November, 2006

Limited Transgene Immune Response and Long-Term Expression of Human α -L-Iduronidase in Young Adult Mice with Mucopolysaccharidosis Type I by Liver-Directed Gene Therapy

C. Di Domenico, D. Di Napoli, E. Gonzalez Y Reyero [...]

Human Gene Therapy