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Abstract

First published 1990-6

Tissue and cellular distribution of alpha-L-iduronidase in the pig.

H Sakuda, A Kusaba, T Ohshita [...]

Journal of Histochemistry & Cytochemistry

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Research article

First published 1996-08

Myoblast Gene Therapy in Canine Mucopolysaccharidosis I: Abrogation by an Immune Response to α - l -Iduronidase

Robert M. Shull, Xiaochen Lu, Michael F. McEntee [...]

Human Gene Therapy

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Research article

First published 1995-09

In Vivo Delivery of Human α - l -Iduronidase in Mice Implanted with Neo-Organs

Anna Salvetti, Philippe Moullier, Véronique Cornet [...]

Human Gene Therapy

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Research article

First published 1999-06

Gene Therapy for Canine alpha-L-Iduronidase Deficiency: In Utero Adoptive Transfer of Genetically Corrected Hematopoietic Progenitors Results in Engraftment but Not Amelioration of Disease

Carolyn Lutzko, Fusayuki Omori, Anthony C. G. Abrams-Ogg [...]

Human Gene Therapy

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Research article

First published 1992-08

Correction of Mucopolysaccharidosis Type I Fibroblasts by Retroviral-Mediated Transfer of the Human α- l -Iduronidase Gene

D. S. Anson, J. Bielicki, J. J. Hopwood

Human Gene Therapy

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Case report

First published 2017-5

Role of rehabilitation in Hurler's syndrome

Sudhir Ramkishore Mishra, Mona Shastri, Jaishree Ramesh

Journal of Back and Musculoskeletal Rehabilitation

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Research article

First published 2009-12

Mutational Analysis of the α-L-Iduronidase Gene in Three Egyptian Families: Identification of Three Novel Mutations and Five Novel Polymorphisms

Khalda Amr, Ahmed Katoury, Mohamed Abdel-Hamid [...]

Genetic Testing and Molecular Biomarkers

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Research article

First published 1999-09

Enzymatic Correction and Cross-Correction of Mucopolysaccharidosis Type I Fibroblasts by Adeno-Associated Virus-Mediated Transduction of the alpha-L-Iduronidase Gene

Seth D. Hartung, Rukmini G. Reddy, Chester B. Whitley [...]

Human Gene Therapy

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Research article

First published 2002-10

In Utero Injection of α -L-Iduronidase-Carrying Retrovirus in Canine Mucopolysaccharidosis Type I: Infection of Multiple Tissues and Neonatal Gene Expression

Lisa Meertens, Yongjun Zhao, Suzana Rosic-Kablar [...]

Human Gene Therapy

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Research article

First published 2006-11

Limited Transgene Immune Response and Long-Term Expression of Human α -L-Iduronidase in Young Adult Mice with Mucopolysaccharidosis Type I by Liver-Directed Gene Therapy

C. Di Domenico, D. Di Napoli, E. Gonzalez Y Reyero [...]

Human Gene Therapy

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