Sage Journals: Discover world-class research

Open access

Research article

First published 2025-5

Visualizing ambulatory performance by age and rates of decline among patients with Duchenne muscular dystrophy

Anna G Mayhew, James Signorovitch, Michaela Johnson [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2024-04-30

Stride Velocity 95 th Centile Detects Decline in Ambulatory Function Over Shorter Intervals than the 6-Minute Walk Test or North Star Ambulatory Assessment in Duchenne Muscular Dystrophy

Michael Rabbia, Maitea Guridi Ormazabal, Hannah Staunton [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2024-12

Safety and effectiveness of ataluren in patients with Duchenne muscular dystrophy: single-center experience from Saudi Arabia

Mushtaha Ahmad, Alaa ElRasoul, Raneem Sedayou [...]

Journal of International Medical Research

Open access

Research article

First published 2021-07-30

Comparison of Long-term Ambulatory Function in Patients with Duchenne Muscular Dystrophy Treated with Eteplirsen and Matched Natural History Controls

Jerry R. Mendell, Navid Khan, Nanshi Sha [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2024-01-02

Quantifying Variability in Motor Function in Duchenne Muscular Dystrophy: UK Centiles for the NorthStar Ambulatory Assessment,10 m Walk Run Velocity and Rise from Floor Velocity in GC Treated Boys

Georgia Stimpson, Deborah Ridout, Amy Wolfe [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2021-09-14

A Randomized,Double-Blind,Placebo-Controlled,Global Phase 3 Study of Edasalonexent in Pediatric Patients with Duchenne Muscular Dystrophy: Results of the PolarisDMD Trial

Richard S. Finkel, Craig M. McDonald, H. Lee Sweeney [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2024-03-05

Characterization of Phenotypic Variability in Becker Muscular Dystrophy for Clinical Practice and Towards Trial Readiness: A Two-Years Follow up Study

Giulia Ricci, Alessandra Govoni, Francesca Torri [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2024-01-02

Findings from the Longitudinal CINRG Becker Natural History Study

Paula R. Clemens, Heather Gordish-Dressman, Gabriela Niizawa [...]

Journal of Neuromuscular Diseases

Open access

Research article

First published 2024-04-30

The Association Between Physical Activity/Heart Rate Variability Data Obtained Using a Wearable Device and Timed Motor Functional Tests in Patients with Duchenne Muscular Dystrophy: A Pilot Study

Akinori Nakamura, Tsuyoshi Matsumura, Yasuhiro Takeshima [...]

Journal of Neuromuscular Diseases

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