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Research article

First published 2021-07-30

Hereditary Transthyretin Amyloidosis- Clinical and Genetic Characteristics of a Multiracial South-East Asian Cohort in Singapore

Zhiyong Chen, Jasmine S. Koh, Monica Saini [...]

Journal of Neuromuscular Diseases

Retricted access

Research article

First published 2018-7

New Medications in the Treatment of Hereditary Transthyretin Amyloidosis

Scot Walker

Hospital Pharmacy

Open access

Review article

First published 2025

Neurological efficacy and safety of RNA therapeutics in hereditary transthyretin amyloidosis: a systematic review and meta-analysis of randomized controlled trials

Maha Sajjad, Rabia Ashraf, Riya Bhagwan [...]

Therapeutic Advances in Cardiovascular Disease

Open access

Research article

First published 2025

Fremanezumab for refractory migraine in patients with hereditary transthyretin amyloidosis: A case series

Joana Fernandes, Sofia Ferreira, Cristina Alves [...]

Cephalalgia Reports

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Research article

First published 2022-3

Specific postoperative complications of vitrectomy in hereditary transthyretin amyloidosis

Pathma Thiagasorupan, Emmanuel Barreau, Gaël Gendron [...]

European Journal of Ophthalmology

Retricted access

Research article

First published 2022-1

Pupillometry: An objective test to assess endocular hereditary transthyretin amyloidosis

João Heitor Marques, Luísa Malheiro, Jorge Malheiro [...]

European Journal of Ophthalmology

Retricted access

Research article

First published 2019-9

Evaluating Prognostic Factors for Liver Transplantation Among United States Patients With Hereditary Transthyretin-Mediated (hATTR) Amyloidosis Using National Registry Data

Danielle Brandman, Hollis Lin, Anastasia McManus [...]

Progress in Transplantation

Open access

Research article

First published 2020-02

Nonclinical Safety Profile of Revusiran,a 1st-Generation GalNAc-siRNA Conjugate for Treatment of Hereditary Transthyretin-Mediated Amyloidosis

Jessica E. Sutherland, Julia L. Hettinger, Amy Chan [...]

Nucleic Acid Therapeutics

Open access

Research article

First published 2020-06

Population Pharmacokinetic–Pharmacodynamic Modeling of Inotersen,an Antisense Oligonucleotide for Treatment of Patients with Hereditary Transthyretin Amyloidosis

Rosie Z. Yu, Jon W. Collins, Shannon Hall [...]

Nucleic Acid Therapeutics

Open access

Research article

First published 2023

De Novo Fibrinogen A Alpha Chain Amyloidosis in a Kidney Transplant Patient: Case Report and Literature Review

Taqui Khaja, Luan Truong, George Nassar

Canadian Journal of Kidney Health and Disease

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