Sage Journals: Discover world-class research

Open access

Brief report

First published 2025

Identification of early changes in multiple biomarkers following CFTR modulator initiation in patients with cystic fibrosis

Pascal Heer, Clara Fernandez Elviro, Angela Koutsokera [...]

Therapeutic Advances in Respiratory Disease

Open access

Research article

First published 2018-2

Use of a High-Throughput Phenotypic Screening Strategy to Identify Amplifiers,a Novel Pharmacological Class of Small Molecules That Exhibit Functional Synergy with Potentiators and Correctors

Kenneth A. Giuliano, Shinichiro Wachi, Lawrence Drew [...]

Journal of Biomolecular Screening

Retricted access

Research article

First published 2017-12

A Homogeneous Cell-Based Halide-Sensitive Yellow Fluorescence Protein Assay to Identify Modulators of the Cystic Fibrosis Transmembrane Conductance Regulator Ion Channel

Emery Smith, Kenneth A. Giuliano, Justin Shumate [...]

ASSAY and Drug Development Technologies

Open access

Research article

First published 2025-10

Implications for cystic fibrosis therapy: Potentiator icenticaftor is superior to ivacaftor in improving function and maintaining stability of F508del CFTR

Deborah M Cholon, Luba A Aleksandrov, Nancy L Quinney [...]

Science Progress

Open access

Review article

First published 2022

New drugs in cystic fibrosis: what has changed in the last decade?

Juliana Roda, Catarina Pinto-Silva, Iris A.I. Silva [...]

Sage Open Chronic Disease

Open access

Review article

First published 2019

The combination of tezacaftor and ivacaftor in the treatment of patients with cystic fibrosis: clinical evidence and future prospects in cystic fibrosis therapy

Sherstin T. Lommatzsch, Jennifer L. Taylor-Cousar

Therapeutic Advances in Respiratory Disease

Retricted access

Review article

First published 2012-7

Cystic Fibrosis Transmembrane Conductance Regulator–Modifying Medications: The Future of Cystic Fibrosis Treatment

Rebecca S Pettit

Annals of Pharmacotherapy

Retricted access

Review article

First published 2020-09

Correction of Airway Stem Cells: Genome Editing Approaches for the Treatment of Cystic Fibrosis

Nicholas E. King, Shingo Suzuki, Cristina Barillà [...]

Human Gene Therapy

Open access

Research article

First published 2024

Perceived burden of respiratory physiotherapy in people with cystic fibrosis taking elexacaftor–tezacaftor–ivacaftor combination: a 1-year observational study

Chiara Blardone, Simone Gambazza, Alessandra Mariani [...]

Therapeutic Advances in Respiratory Disease

Retricted access

Research article

First published 2016-01

Long-Term Expression of the Human CFTR Gene in Mouse Airway via Helper-Dependent Adenoviral Vector Delivery and Transient Immunosuppression

Huibi Cao, Jing Wu, Cathleen Duan [...]

Human Gene Therapy

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