Sage Journals: Discover world-class research

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Meeting report

First published 2023-10

An Overview of Nonclinical and Clinical Liver Toxicity Associated With AAV Gene Therapy

Laurence O. Whiteley

Toxicologic Pathology

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Research article

First published 2026-5

A Tripartite AAV System with Engineered Lox Sites Enables Efficient Delivery of the EYS Gene for Retinal Gene Therapy

Kun-Do Rhee, Poppy Datta, Clairissa Baccam [...]

Human Gene Therapy

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Research article

First published 2007-02

Functions of AAV-CMV-F.IX And AAV-EF1α-F.IX in Gene Therapy for Hemophilia B

Viroj Wiwanitkit

Human Gene Therapy

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Research article

First published 2024-07

Leveraging CRISPR-Cas9 for Accurate Detection of AAV-Neutralizing Antibodies: The AAV-HDR Method

Guohua Li, Saining Tian, Xinyu Sun [...]

Human Gene Therapy

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Research article

First published 2003-2

Platelet-derived growth factor-producing cells immortalized from rat mesencephalon with SV40 large T antigen transduced by an AAV vector

André W. Phillips, Peisu Zhang, Mary Ellen Truckenmiller [...]

Restorative Neurology and Neuroscience

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Research article

First published 2015-04

AAV-8 Is More Efficient than AAV-9 in Transducing Neonatal Dog Heart

Xiufang Pan, Yongping Yue, Keqing Zhang [...]

Human Gene Therapy Methods (Part B)

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Review article

First published 2026

Adeno-associated virus (AAV) mediated advanced therapeutic interventions for inherited and non-inherited cardiac disorders

Indu Singh, Anil Kumar, Awdhesh Kumar Chaudhary [...]

Journal of the Renin-Angiotensin-Aldosterone System

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Research article

First published 2024-12

Neuropathological Findings in Nonclinical Species Following Administration of Adeno-Associated Virus (AAV)-Based Gene Therapy Vectors

Brad Bolon, Elizabeth Buza, Elizabeth Galbreath [...]

Toxicologic Pathology

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Research article

First published 2016-06

AAV Natural Infection Induces Broad Cross-Neutralizing Antibody Responses to Multiple AAV Serotypes in Chimpanzees

Roberto Calcedo, James M. Wilson

Human Gene Therapy Clinical Development

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Research article

First published 2026-3

Multivariate Process Optimization for Fixed-Bed Bioreactor-Based AAV Production Improves Total Batch Yield

Ruchita Selot, Ashish Khaparde, Sharath Babu G.R. [...]

Human Gene Therapy

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