Search results: Sage Journals

Restricted accessResearch articleFirst published April, 2016

Intracellular Trafficking of AAV5 Vectors

Balaji Balakrishnan, Giridhara R. Jayandharan

Human Gene Therapy Methods (Part B)

Restricted accessResearch articleFirst published December, 2025

Biacore Analysis of Cross-Reactive Adeno-Associated Virus Antibodies in Monkeys Following Intravenous Administration of AAV5,AAV8,and AAV9 Vectors

Yanshan Dai, Glen Banks, Grace Wu [...]

Human Gene Therapy

Open accessResearch articleFirst published January, 2024

Prophylactic Prednisolone Promotes AAV5 Hepatocyte Transduction Through the Novel Mechanism of AAV5 Coreceptor Platelet-Derived Growth Factor Receptor Alpha Upregulation and Innate Immune Suppression

Britta Handyside, Lening Zhang, Bridget Yates [...]

Human Gene Therapy

Restricted accessResearch articleFirst published February, 2022

Genetic Modification of the AAV5 Capsid with Lysine Residues Results in a Lung-Tropic Liver-Detargeted Gene Transfer Vector

Katie M. Stiles, Esther Z. Frenk, Stephen M. Kaminsky [...]

Human Gene Therapy

Restricted accessResearch articleFirst published December, 2017

Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3 -Mutant Dogs

Guo-jie Ye, András M. Komáromy, Caroline Zeiss [...]

Human Gene Therapy Clinical Development

Restricted accessResearch articleFirst published October, 2024

AAV5 Delivery of CRISPR/Cas9 Mediates Genome Editing in the Lungs of Young Rhesus Monkeys

Shun-Qing Liang, Andrew W. Navia, Michelle Ramseier [...]

Human Gene Therapy

Restricted accessResearch articleFirst published October, 2015

OneBac 2.0: Sf 9 Cell Lines for Production of AAV5 Vectors with Enhanced Infectivity and Minimal Encapsidation of Foreign DNA

Mario Mietzsch, Vincent Casteleyn, Stefan Weger [...]

Human Gene Therapy

Restricted accessResearch articleFirst published January, 2020

Sustained Interleukin-10 Transgene Expression Following Intra-Articular AAV5-IL-10 Administration to Horses

Kaitlyn L. Moss, Zibin Jiang, Michael E. Dodson [...]

Human Gene Therapy

Restricted accessResearch articleFirst published September, 2017

A Preclinical Study in Rhesus Macaques for Cystic Fibrosis to Assess Gene Transfer and Transduction by AAV1 and AAV5 with a Dual-Luciferase Reporter System

William B. Guggino, Janet Benson, JeanClare Seagrave [...]

Human Gene Therapy Clinical Development

Open accessResearch articleFirst published April, 2022

Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A

Robert Klamroth, Gregory Hayes, Tatiana Andreeva [...]

Human Gene Therapy

Restricted accessResearch articleFirst published April, 2016

Intracellular Trafficking of AAV5 Vectors

Balaji Balakrishnan, Giridhara R. Jayandharan

Human Gene Therapy Methods (Part B)

Restricted accessResearch articleFirst published December, 2025

Biacore Analysis of Cross-Reactive Adeno-Associated Virus Antibodies in Monkeys Following Intravenous Administration of AAV5,AAV8,and AAV9 Vectors

Yanshan Dai, Glen Banks, Grace Wu [...]

Human Gene Therapy

Open accessResearch articleFirst published January, 2024

Prophylactic Prednisolone Promotes AAV5 Hepatocyte Transduction Through the Novel Mechanism of AAV5 Coreceptor Platelet-Derived Growth Factor Receptor Alpha Upregulation and Innate Immune Suppression

Britta Handyside, Lening Zhang, Bridget Yates [...]

Human Gene Therapy

Restricted accessResearch articleFirst published February, 2022

Genetic Modification of the AAV5 Capsid with Lysine Residues Results in a Lung-Tropic Liver-Detargeted Gene Transfer Vector

Katie M. Stiles, Esther Z. Frenk, Stephen M. Kaminsky [...]

Human Gene Therapy

Restricted accessResearch articleFirst published December, 2017

Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3 -Mutant Dogs

Guo-jie Ye, András M. Komáromy, Caroline Zeiss [...]

Human Gene Therapy Clinical Development

Restricted accessResearch articleFirst published October, 2024

AAV5 Delivery of CRISPR/Cas9 Mediates Genome Editing in the Lungs of Young Rhesus Monkeys

Shun-Qing Liang, Andrew W. Navia, Michelle Ramseier [...]

Human Gene Therapy

Restricted accessResearch articleFirst published October, 2015

OneBac 2.0: Sf 9 Cell Lines for Production of AAV5 Vectors with Enhanced Infectivity and Minimal Encapsidation of Foreign DNA

Mario Mietzsch, Vincent Casteleyn, Stefan Weger [...]

Human Gene Therapy

Restricted accessResearch articleFirst published January, 2020

Sustained Interleukin-10 Transgene Expression Following Intra-Articular AAV5-IL-10 Administration to Horses

Kaitlyn L. Moss, Zibin Jiang, Michael E. Dodson [...]

Human Gene Therapy

Restricted accessResearch articleFirst published September, 2017

A Preclinical Study in Rhesus Macaques for Cystic Fibrosis to Assess Gene Transfer and Transduction by AAV1 and AAV5 with a Dual-Luciferase Reporter System

William B. Guggino, Janet Benson, JeanClare Seagrave [...]

Human Gene Therapy Clinical Development

Open accessResearch articleFirst published April, 2022

Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A

Robert Klamroth, Gregory Hayes, Tatiana Andreeva [...]

Human Gene Therapy