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Research article

First published 2016-04

Intracellular Trafficking of AAV5 Vectors

Balaji Balakrishnan, Giridhara R. Jayandharan

Human Gene Therapy Methods (Part B)

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Research article

First published 2025-12

Biacore Analysis of Cross-Reactive Adeno-Associated Virus Antibodies in Monkeys Following Intravenous Administration of AAV5,AAV8,and AAV9 Vectors

Yanshan Dai, Glen Banks, Grace Wu [...]

Human Gene Therapy

Open access

Research article

First published 2024-01

Prophylactic Prednisolone Promotes AAV5 Hepatocyte Transduction Through the Novel Mechanism of AAV5 Coreceptor Platelet-Derived Growth Factor Receptor Alpha Upregulation and Innate Immune Suppression

Britta Handyside, Lening Zhang, Bridget Yates [...]

Human Gene Therapy

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Research article

First published 2022-02

Genetic Modification of the AAV5 Capsid with Lysine Residues Results in a Lung-Tropic Liver-Detargeted Gene Transfer Vector

Katie M. Stiles, Esther Z. Frenk, Stephen M. Kaminsky [...]

Human Gene Therapy

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Research article

First published 2017-12

Safety and Efficacy of AAV5 Vectors Expressing Human or Canine CNGB3 in CNGB3 -Mutant Dogs

Guo-jie Ye, András M. Komáromy, Caroline Zeiss [...]

Human Gene Therapy Clinical Development

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Research article

First published 2024-10

AAV5 Delivery of CRISPR/Cas9 Mediates Genome Editing in the Lungs of Young Rhesus Monkeys

Shun-Qing Liang, Andrew W. Navia, Michelle Ramseier [...]

Human Gene Therapy

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Research article

First published 2015-10

OneBac 2.0: Sf 9 Cell Lines for Production of AAV5 Vectors with Enhanced Infectivity and Minimal Encapsidation of Foreign DNA

Mario Mietzsch, Vincent Casteleyn, Stefan Weger [...]

Human Gene Therapy

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Research article

First published 2017-09

A Preclinical Study in Rhesus Macaques for Cystic Fibrosis to Assess Gene Transfer and Transduction by AAV1 and AAV5 with a Dual-Luciferase Reporter System

William B. Guggino, Janet Benson, JeanClare Seagrave [...]

Human Gene Therapy Clinical Development

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Research article

First published 2020-01

Sustained Interleukin-10 Transgene Expression Following Intra-Articular AAV5-IL-10 Administration to Horses

Kaitlyn L. Moss, Zibin Jiang, Michael E. Dodson [...]

Human Gene Therapy

Open access

Research article

First published 2022-04

Global Seroprevalence of Pre-existing Immunity Against AAV5 and Other AAV Serotypes in People with Hemophilia A

Robert Klamroth, Gregory Hayes, Tatiana Andreeva [...]

Human Gene Therapy

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