Sage Journals: Discover world-class research

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Review article

First published 2025-12

The β-Hemoglobinopathies as a Model for the Development of Nonviral,Episomal Vectors for Gene Therapy

Aglaia Athanassiadou, Argyro Sgourou, Meletios Verras

Human Gene Therapy

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Case report

First published 2005-9

Glycemic Monitoring in Diabetics with Sickle Cell Plus β-Thalassemia Hemoglobinopathy

Sheri M Kosecki, Philip T Rodgers, Martha B Adams

Annals of Pharmacotherapy

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Research article

First published 2021-04

Universal Gene Correction Approaches for β-hemoglobinopathies Using CRISPR-Cas9 and Adeno-Associated Virus Serotype 6 Donor Templates

Andrés Lamsfus-Calle, Alberto Daniel-Moreno, Guillermo Ureña-Bailén [...]

The CRISPR Journal

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Review article

First published 2016-02

Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β A(T87Q) - Globin Gene

Olivier Negre, Anne-Virginie Eggimann, Yves Beuzard [...]

Human Gene Therapy

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Research article

First published 2015-8

Cell signaling pathways involved in drug-mediated fetal hemoglobin induction: Strategies to treat sickle cell disease

Betty S Pace, Li Liu, Biaoru Li [...]

Experimental Biology and Medicine

Open access

Case report

First published 2021

Fat Embolism Syndrome in Sickle Cell β-Thalassemia Patient With Osteonecrosis: An Uncommon Presentation in a Young Adult

Vikram Sangani, Mytri Pokal, Mamtha Balla [...]

Journal of Investigative Medicine High Impact Case Reports

Open access

Research article

First published 2023-02

Automated Good Manufacturing Practice-Compatible CRISPR-Cas9 Editing of Hematopoietic Stem and Progenitor Cells for Clinical Treatment of β-Hemoglobinopathies

Guillermo Ureña-Bailén, Milena Block, Tommaso Grandi [...]

The CRISPR Journal

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Research article

First published 2015-3

Spectrum of Hemoglobinopathies Among the Primitive Tribes

Dipika Mohanty, Malay B. Mukherjee, Roshan B. Colah [...]

Asia Pacific Journal of Public Health

Open access

Research article

First published 2018-02

Rapid and Sensitive Assessment of Globin Chains for Gene and Cell Therapy of Hemoglobinopathies

Constantinos C. Loucari, Petros Patsali, Thamar B. van Dijk [...]

Human Gene Therapy Methods (Part B)

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Other

First published 1981-03

Laboratory Identification of Inherited Hemoglobinopathies in Children

Haewon C. Kim

Clinical Pediatrics

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