Editorial board

Rashmi Gopal-Srivastava, PhD National Institutes of Health, USA
Alan K. Percy, MD University of Alabama School of Medicine, USA

Stephen C. Groft, Pharm D National Institutes of Health, USA
Kenjiro Kosaki, MD Keio University School of Medicine, Japan

Shivarajan Manickavasagam Amudhavalli, MBBS, FACMG,FAAP Children's Mercy Hospital, Kansas City, MO, USA
Xinhua Bao, MD Peking University First Hospital, China
Lindsay Burrage, MD, PhD Baylor College of Medicine, Houston, TX, USA
John Christodoulou, MB, PhD Murdoch Childrens Research Institute. Australia
Angus Clarke, BM, DM, MRCP Cardiff University, UK
Alison G. Compton, PhD Murdoch Children's Research Institute, Parkville, VIC, Australia
Simon Day, PhD NDA Group, UK
Marni J. Falk, MD The Children's Hospital of Philadelphia and University of Pennsylvania Perelman School of Medicine, Philadelphia, PA, USA
Carlos Ferreira, MD National Human Genome Research Institute, USA
Ann E. Frazier, PhD Murdoch Children's Research Institute, Parkville, VIC, Australia
Meral Gunay-Aygun, MD National Human Genome Research Institute, USA
Melissa Haendel, MD University of Colorado Anschutz Medical Campus, USA
Bruce Korf, MD, PhD University of Alabama Birmingham, USA
Michele Manion, BS Primary Ciliary Dyskinesia Foundation, USA
Chuck Mohan, BS United Mitochondrial Disease Foundation, USA
Sandesh C.S. Nagamani, MBBS, MD Baylor College of Medicine, Houston, TX, USA
Dan O'Connor, MD, PhD The Association of the British Pharmaceutical Industry, London, UK
Sarah E. O’Kelley, PhD University of Alabama at Birmingham, USA
Phillip L. Pearl, MD Boston Children's Hospital, USA
Ratna Puri, MD, DM Sir Ganga Ram Hospital, India
Harsha K. Rajasimha, MS, PhD Indo US Organization for Rare Diseases, USA
Marco Roos, PhD Leiden University Medical Centre, The Netherlands
Ola Skjeldal, MD, PhD Rikshospitalet University Hospital, Norway
Marshall Summar, MD Children’s National Hospital, USA
John L.P. Thompson, PhD Columbia University, USA
Bruce Trapnell, MD CCHMC, USA
Nicole Van Bergen, BSc (Hon), PhD Murdoch Children's Research Institute, Parkville, VIC, Australia
Carla M.L. van Herpen, MD, PhD Radboud University Medical Center, The Netherlands
Wendy A.G. van Zelst-Stams, MD, PhD Radboud University Medical Center, The Netherlands
Laurent Villard, PhD INSERM and Aix Marseille University, France