Editorial board

Tiina Urv PhD Division of Rare Diseases Research Innovation, National Center for Advancing Translational Sciences, NIH, Bethesda, USA

Mahima Dua SAGE Publishing, New Delhi, India

Claudia A. Chiriboga MD, MPH Columbia University Irving Medical Center, New York, USA
Maya Chopra, MBBS, FRACP Boston Children’s Hospital, Harvard Medical School, Boston, MA, USA
Larissa Kerecuk MBBS, BSc Birmingham Women’s and Children’s NHS Foundation Trust, Birmingham, UK
Jemima Mellerio MD St John’s Institute of Dermatology, Guy’s and St Thomas’ NHS Foundation Trust, London, UK
Katrin Õunap MD, PhD University of Tartu and Tartu University Hospital, Tartu, Estonia
David Pearce, PhD Sanford School of Medicine of the University of South Dakota, Sioux Falls, SD, USA
Maurizio Scarpa MD, PhD Center for Rare Diseases, Udine University Hospital, Udine, Italy
Marcela Votruba BM BCh, BA, MA Vision Sciences, Cardiff University, UK

Annemieke Aartsma-Rus PhD Leiden University Medical Center, Leiden, The Netherlands
Dionysios Alexandrou MD MD Res Moorfields Hospital NHS Trust, London, UK
Guilherme Baldo PharmD PhD Hospital de Clinicas de Porto Alegre, Porto Alegre, Brazil
John Bladen BSc PhD Kings College Hospital NHS Foundation Trust, London, UK
Roberto Giugliani MD PhD MSc Hospital de Clinicas de Porto Alegre, Porto Alegre, Brazil
Andrea Gropman, MD St. Jude Children's Research Hospital, Memphis, TN, USA
Jeanine Jarnes PharmD BCOP BCPS University of Minnesota, MN, USA
Mariya Moosajee BSc PhD University College London, London, UK
Mukund Nori BSc MSc PhD rareLife solutions, South Norwalk, CT, USA
Daniele Orsucci MD Unit of Neurology, San Luca Hospital, Lucca, Italy
Arrigo Schieppati MD PhD Rare Disease Unit, Ospedale Papa Giovanni XXIII, Bergamo, Italy
Willeke van Roon-Mom PhD Leiden University Medical Center, Leiden, The Netherlands

Jasmin Barman-Aksözen International Porphyria Patient Network, Zurich, Switzerland
Daniel O’Reilly RNA Therapeutics Institute, UMass Medical School, MA, USA
Simon Stones Collaboro Consulting, Manchester, UK
Russell Wheeler Leber's Hereditary Optic Neuropathy Society, UK
Laurence Woollard On The Pulse Consultancy Ltd, Cambridge, UK

Goksel Altinisik, MD Chest Department, Pamukkale University, Denizli, Turkey
Malaka Ameratunga, MBBS, PhD, FRACP School of Translational Medicine, Monash University, Melbourne, Australia
Nahya Awada, McR, PhD Carleton University, Canada
Andrej Belancic Department of Basic and Clinical Pharmacology and Toxicology, University of Rijeka, Rijeka, Croatia
Shein-Chung Chow, PhD Duke University School of Medicine, Durham, NC, USA
Kristen Cribbs, PhD, MPH Alkemi LLC, Manchester Center, VT, USA
Dr. Zainab Fatima, MBBS Shaikh Khalifa bin Zayed Al-Nahyan Medical and Dental College, Pakistan
Brandy E. Fureman, PhD Epilepsy Foundation, Bowie, MD, USA
Mohammad-Salar Hosseini, MD, MPH Tabriz University of Medical Sciences, Tabriz, Iran
Jorge M. Mendes, PhD, Habilitation Comprehensive Health Research Centre (CHRC), NOVA Medical School, Lisbon, Portugal
Himanshu Narayan Singh ,M Tech, PhD Memorial Sloan Kettering Cancer Center, New York, USA
Vadim Zakiev, MD Pirogov Russian National Research Medical University, Russia