KohnDB, HershfieldMS, PuckJM, AiutiA, BlincoeA, GasparHB, NotarangeloLD and GrunebaumE. (2018). Consensus approach for the management of severe combined immune deficiency caused by adenosine deaminase deficiency. J Allergy Clin Immunol, 143:852–863.
2.
KohnDB, MS HershfieldD C, arbonaroA S, higeokaJ B, rooksEM, SmogorzewskaLW, BarskyR C, hanF Burotto, et al. (1998). T lymphocytes with a normal ADA gene accumulate after transplantation of transduced autologous umbilical cord blood CD34+ cells in ADA-deficient SCID neonates. Nat Med, 4:775–780.
3.
KohnDB, KI WeinbergJA, NoltaLN, HeissC L, enarskyGM, CrooksME, HanleyG A, nnettJSBrooks, et al. (1995). Engraftment of gene-modified umbilical cord blood cells in neonates with adenosine deaminase deficiency. Nat Med, 1:1017–1023.
