BioMarin Pharmaceutical. 2016. BioMarin provides positive proof-of-concept data for BMN 270 gene therapy in hemophilia A in late breaking oral presentation at the World Federation of Hemophilia (WFH) 2016 World Congress. Available at: http://investors.bmrn.com/releasedetail.cfm?ReleaseID=981465 (accessed August1, 2016).
Ziopharm Oncology. 2016. Ziopharm issues statement regarding phase I study of gene therapy candidate Ad-RTS-hIL-12 in brain cancer. Available at: http://ir.ziopharm.com/releasedetail.cfm?ReleaseID=979750 (accessed August1, 2016).
8.
Ziopharm Oncology. 2016. Ziopharm provides update regarding phase I study of gene therapy candidate Ad-RTS-hIL-12 in brain cancer. Available at: http://ir.ziopharm.com/releasedetail.cfm?ReleaseID=980076 (accessed August1, 2016).
Spark Therapeutics and Pfizer. 2016. Spark Therapeutics and Pfizer announce updated data from first cohort in hemophilia B phase 1/2 trial demonstrating consistent, sustained therapeutic levels of factor IX activity. Available at: http://ir.sparktx.com/phoenix.zhtml?c=253900&p=irol-newsArticle&ID=2187752 (accessed August5, 2016).