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References
1.Voyager Therapeutics . Voyager Provides Update on SOD1 ALS Gene Therapy Program . February 11, 2025 . Available from: https://ir.voyagertherapeutics.com/news-releases/news-release-details/voyager-provides-update-sod1-als-gene-therapy-program [Last accessed:
February 13 , 2025
].
2.Encoded Therapeutics . Encoded Therapeutics Reports Clinical Progress of ETX101 Gene Therapy for Dravet Syndrome, Recaps 2024 Corporate Achievements and Provides 2025 Outlook . February 13, 2025 . Available from: https://encoded.com/press-releases/encoded-therapeutics-reports-clinical-progress-of-etx101-gene-therapy-for-dravet-syndrome-recaps-2024-corporate-achievements-and-provides-2025-outlook/ [Last accessed:
February 14 , 2025
].
3.Fractyl Health . Form 8-K filed with the U.S. Securities and Exchange Commission . January 31, 2025 . Available from: https://ir.fractyl.com/static-files/60e27f27-231d-40bc-b0c2-9c7dad09b48d [Last accessed:
February 14 , 2025
].
4.
Thomas
U
. ExpressionEdits Partners with Boehringer to Enhance Gene Therapies with AI-Based Intron Design . Genetic Engineering & Biotechnology News . February 12, 2025 . Available from: https://www.genengnews.com/topics/genome-editing/expressionedits-partners-with-boehringer-to-enhance-gene-therapies-with-ai-based-intron-design/ [Last accessed:
February 13 , 2025
].
5.ExpressionEdits. ExpressionEdits Collaborates with Boehringer Ingelheim to Develop Enhanced Gene Therapies . February 12, 2025 . Available from: https://www.businesswire.com/news/home/20250212036713/en/ExpressionEdits-Collaborates-with-Boehringer-Ingelheim-to-Develop-Enhanced-Gene-Therapies [Last accessed:
February 13 , 2025
].
6.RhyGaze . Institute of Molecular and Clinical Ophthalmology Basel Spinout RhyGaze Closes USD 86 Million Series A Round to Further Novel Gene Therapy for Vision Restoration . January 10, 2025 . Available from: https://www.businesswire.com/news/home/20250110360650/en/Institute-of-Molecular-and-Clinical-Ophthalmology-Basel-Spinout-RhyGaze-Closes-USD-86-Million-Series-A-Round-to-Further-Novel-Gene-Therapy-for-Vision-Restoration [Last accessed:
February 13 , 2025
].
7.Sarepta Therapeutics . Sarepta Therapeutics Announces Results from Part 2 of the EMBARK Study Demonstrating Sustained Benefits and Disease Stabilization in Ambulatory Individuals with Duchenne Muscular Dystrophy Following Treatment with ELEVIDYS . January 27, 2025 . Available from: https://investorrelations.sarepta.com/news-releases/news-release-details/sarepta-therapeutics-announces-results-part-2-embark-study [Last accessed:
February 13 , 2025
].
8.Rentschler Biopharma . Rentschler Biopharma announces strategic realignment of its global business operations . January 30, 2025 . Available from: https://www.rentschler-biopharma.com/en-us/news-events/press-releases/rentschler-biopharma-announces-strategic-realignment-of-its-global-business-operations/ [Last accessed:
February 13 , 2025
].
9.Genethon . Genethon and Eukarÿs announce a strategic partnership to develop a breakthrough technology to reduce the biomanufacturing cost of gene therapies . January 23, 2025 . Available from: https://www.genethon.com/genethon-and-eukarys-announce-a-strategic-partnership-to-develop-a-breakthrough-technology-to-reduce-the-biomanufacturing-cost-of-gene-therapies/ [Last accessed:
February 13 , 2025
].
