AmiracheF, LévyC, CostaC, et al.Mystery solved: VSV-G-LVs do not allow efficient gene transfer into unstimulated T cells, B cells, and HSCs because they lack the LDL receptor. Blood, 2014; 123:1422–1424.
2.
HumbertO, ChanF, RajawatYS, et al.Rapid immune reconstitution of SCID-X1 canines after G-CSF/AMD3100 mobilization and in vivo gene therapy. Blood Adv, 2018; 2:987–999.
3.
VerhoeyenE, RodríguezFJ, CossetFL, et al.Gene therapy in Fanconi anemia: a matter of time, safety and gene transfer tool efficiency. Curr Gene Ther, 2017; 16:297–308
4.
MhaidlyR, VerhoeyenE. The future: in vivo CAR T cell gene therapy. Mol Ther, 2019; 27:707–709.
5.
FrankAM, BraunAH, ScheibL, et al.Combining T-cell-specific activation and in vivo gene delivery through CD3-targeted lentiviral vectors. Blood Adv, 2020; 4:5702–5715.
