AbstractGet full access to this articleView all access options for this article.Get accessReferences1. Wang J-H et al. Adeno-associated virus as a delivery vector for gene therapy of human diseases. Signal Transduction and Targeted Therapy (2024) 9:78. (https://doi.org/10.1038/s41392-024-01780-w).2.https://www.fda.gov/news-events/press-announcements/fda-approves-first-gene-therapy-treatment-aromatic-l-amino-acid-decarboxylase-deficiency.3.https://www.genengnews.com/topics/drug-discovery/aav-gene-therapy-for-lca1-improves-vision-dramatically/.
