Sage Journals: Discover world-class research

Free access

Review article

First published 2010-10

Review: Therapeutic approaches for lysosomal storage diseases

Gregory M. Pastores

Therapeutic Advances in Endocrinology and Metabolism

Open access

Research article

First published 2016

Small Molecules

Saida Ortolano

Journal of Inborn Errors of Metabolism and Screening

Retricted access

Research article

First published 2023-3

A Systematic Review and Meta-analyses of Longitudinal Studies on Drug Treatments for Gaucher Disease

Letícia Paula Leonart, Mariana M. Fachi, Beatriz Böger [...]

Annals of Pharmacotherapy

Retricted access

Research article

First published 2022-9

Cell cycle disturbances in mucopolysaccharidoses: Transcriptomic and experimental studies on cellular models

Joanna Brokowska, Lidia Gaffke, Karolina Pierzynowska [...]

Experimental Biology and Medicine

Retricted access

Research article

First published 2013-9

Gaucher Disease and Its Treatment Options

Lunawati L. Bennett, Devipriya Mohan

Annals of Pharmacotherapy

Retricted access

Research article

First published 2016-7

Enzyme Replacement or Substrate Reduction? A Review of Gaucher Disease Treatment Options

Alison Van Rossum, Megan Holsopple

Hospital Pharmacy

Retricted access

Review article

First published 2015-03

A Review of Gene Therapy in Canine and Feline Models of Lysosomal Storage Disorders

Allison M. Bradbury, Brittney L. Gurda, Margret L. Casal [...]

Human Gene Therapy Clinical Development

Retricted access

Article commentary

First published 2021-02

Commentary on Some Recent Theses Relevant to Combating Aging: February 2021

Benjamin Zealley, Aubrey D.N.J. de Grey

Rejuvenation Research

Retricted access

Review article

First published 2015-09

The Use of SGLT-2 Inhibitors in Type 2 Diabetes and Heart Failure

Kayla Riggs, Hiba Ali, Heinrich Taegtmeyer [...]

Metabolic Syndrome and Related Disorders

Retricted access

Research article

First published 2006-06

Emerging Strategies for the Treatment of Hereditary Metabolic Storage Disorders

Roscoe O. Brady

Rejuvenation Research

Search results