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Open access

Article commentary

First published 2024

Synergistic Effect of an Antisense Oligonucleotide and Small Molecule on Splicing Correction of the Spinal Muscular Atrophy Gene

Eric W Ottesen, Ravindra N Singh

Neuroscience Insights

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Research article

First published 2024-06

Splice-Switching Antisense Oligonucleotides Correct Phenylalanine Hydroxylase Exon 11 Skipping Defects and Rescue Enzyme Activity in Phenylketonuria

Ainhoa Martínez-Pizarro, Mar álvarez, Maja Dembic [...]

Nucleic Acid Therapeutics

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Research article

First published 2018-9

Chitosan enhances gene delivery of oligonucleotide complexes with magnetic nanoparticles–cell-penetrating peptide

Moataz Dowaidar, Hani Nasser Abdelhamid, Mattias Hällbrink [...]

Journal of Biomaterials Applications

Open access

Review article

First published 2016

Therapeutic Potential of Tricyclo-DNA antisense oligonucleotides

Aurelie Goyenvalle, Christian Leumann, Luis Garcia

Journal of Neuromuscular Diseases

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Research article

First published 2009-03

Noncovalent Peptide-Mediated Delivery of Chemically Modified Steric Block Oligonucleotides Promotes Splice Correction: Quantitative Analysis of Uptake and Biological Effect

Sandra D. Laufer, Anna Lena Recke, Sandra Veldhoen [...]

Nucleic Acid Therapeutics

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Review article

First published 2009-03

Therapeutic Potential of Splice-Switching Oligonucleotides

John Bauman, Natee Jearawiriyapaisarn, Ryszard Kole

Nucleic Acid Therapeutics

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Review article

First published 2022-06

Modulation of RNA Splicing by Oligonucleotides: Mechanisms of Action and Therapeutic Implications

Olga V. Sergeeva, Evgeniya Y. Shcherbinina, Noam Shomron [...]

Nucleic Acid Therapeutics

Open access

Review article

First published 2014-02

Exon-Skipping Antisense Oligonucleotides to Correct Missplicing in Neurogenetic Diseases

Kavitha Siva, Giuseppina Covello, Michela A. Denti

Nucleic Acid Therapeutics

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Brief report

First published 2010-04

The Biological Effect of an Antisense Oligonucleotide Depends on Its Route of Endocytosis and Trafficking

Md. Rowshon Alam, Xin Ming, Vidula Dixit [...]

Nucleic Acid Therapeutics

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Research article

First published 2003-06

Effects of Base Modifications on Antisense Properties of 2′- O -Methoxyethyl and PNA Oligonucleotides

Peter Sazani, Anna Astriab-Fischer, Ryszard Kole

Nucleic Acid Therapeutics

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