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Research article

First published 2003-06

Pathways of Removal of Free DNA Vector Ends in Normal and DNA-PKcs–Deficient SCID Mouse Hepatocytes Transduced with rAAV Vectors

Hiroyuki Nakai, Theresa A. Storm, Sally Fuess [...]

Human Gene Therapy

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Review article

First published 2016-04

Development of rAAV2-CFTR: History of the First rAAV Vector Product to be Used in Humans

Heather S. Loring, Mai K. ElMallah, Terence R. Flotte

Human Gene Therapy Methods (Part B)

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Research article

First published 2017-1

New cell engineering approaches for cartilage regenerative medicine

Magali Cucchiarini

Bio-Medical Materials and Engineering

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Review article

First published 2025-6

Mutagenesis and Carcinogenesis Risk Evaluation for AAV and Lentiviral Gene Therapies

Toufan Parman, Daniella M. Pizzurro, Jacquelynn Lucas [...]

International Journal of Toxicology

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Research article

First published 2024-4

Locally Directed Recombinant Adeno- Associated Virus–Mediated IGF-1 Gene Therapy Enhances Osteochondral Repair and Counteracts Early Osteoarthritis In Vivo

Carolin Peifer, Tamás Oláh, Jagadeesh K. Venkatesan [...]

The American Journal of Sports Medicine

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Research article

First published 2006-8

Enhanced Gene Transfer Efficiency in the Murine Striatum and an Orthotopic Glioblastoma Tumor Model,Using AAV-7- and AAV-8-Pseudotyped Vectors

Thomas C. Harding, Peter J. Dickinson, Byron N. Roberts [...]

Human Gene Therapy

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Research article

First published 2014-08

Efficient Production of Dual Recombinant Adeno-Associated Viral Vectors for Factor VIII Delivery

Qizhao Wang, Biao Dong, Jenni Firrman [...]

Human Gene Therapy Methods (Part B)

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Research article

First published 1999-07

Purification of Recombinant Adeno-Associated Virus by Iodixanol Gradient Ultracentrifugation Allows Rapid and Reproducible Preparation of Vector Stocks for Gene Transfer in the Nervous System

Wim T.J.M.C. Hermens, Olivier Ter Brake, Paul A. Dijkhuizen [...]

Human Gene Therapy

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Review article

First published 2020-11

Bound Protein- and Peptide-Based Strategies for Adeno-Associated Virus Vector-Mediated Gene Therapy: Where Do We Stand Now?

Xintao Zhang, Zheng Chai, R. Jude Samulski [...]

Human Gene Therapy

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Research article

First published 2005-05

Production of Recombinant Adeno-Associated Virus Vectors

S. Zolotukhin

Human Gene Therapy

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