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Research article

First published 1995-09

Nonviral Gene Therapy: The Promise of Genes as Pharmaceutical Products

Fred D. Ledley

Human Gene Therapy

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Review article

First published 2019-09

The Landscape of Cellular and Gene Therapy Products: Authorization,Discontinuations,and Cost

Vaishali Shukla, Enrique Seoane-Vazquez, Souhiela Fawaz [...]

Human Gene Therapy Clinical Development

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Review article

First published 2023-09

Advances and Challenges in the Development of Gene Therapy Medicinal Products for Rare Diseases

Juan A. Bueren, Alberto Auricchio

Human Gene Therapy

Open access

Research article

First published 2017-08

Development of the First World Health Organization Lentiviral Vector Standard: Toward the Production Control and Standardization of Lentivirus-Based Gene Therapy Products

Yuan Zhao, Hannah Stepto, Christian K Schneider

Human Gene Therapy Methods (Part B)

Free access

Research article

First published 2022-09

FDA Guidance on Shedding and Environmental Impact in Clinical Trials Involving Gene Therapy Products

Daniel Eisenman, Scott Swindle

Applied Biosafety

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Research article

First published 2016-09

Optimizing Transgene Configuration and Protein Fusions to Maximize Dopamine Production for the Gene Therapy of Parkinson's Disease

Hannah J. Stewart, G. Scott Ralph, Liang Fong-Wong [...]

Human Gene Therapy Clinical Development

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Review article

First published 2026-5

A comprehensive review of humanized mice applications in regulatory submissions for cell and gene therapy products

Giovanni Pellegrini, Lucia Minoli, Sara Degl’Innocenti [...]

Veterinary Pathology

Open access

Research article

First published 2014-11

Establishment of a Novel Cell Line for the Enhanced Production of Recombinant Adeno-Associated Virus Vectors for Gene Therapy

Stifani Satkunanathan, Jun Wheeler, Robin Thorpe [...]

Human Gene Therapy

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Research article

First published 2018-02

The First Approved Gene Therapy Product for Cancer Ad- p53 (Gendicine): 12 Years in the Clinic

Wei-Wei Zhang, Longjiang Li, Dinggang Li [...]

Human Gene Therapy

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Other

First published 2015-1

Advanced therapy medicinal products: Gene therapy

Antonio Ayala, Mario Muñoz, Sandro Argüelles [...]

Pharmaceuticals Policy and Law

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