Search results

Articles (5)

Journals (0)

1-5 of 5 results for anti-ERT antibodies

Sort by:

Relevance

Select all

Sort by:

Relevance

Retricted access

Research article

First published 2015-01

Enhanced Efficacy from Gene Therapy in Pompe Disease Using Coreceptor Blockade

Sang-oh Han, Songtao Li, Elizabeth D. Brooks [...]

Human Gene Therapy

Open access

Research article

First published 2025

Systemic inflammation in Fabry disease: a longitudinal immuno-genetic analysis based on variant stratification

Haylen Marín Gómez, Miguel López-Garrido

Therapeutic Advances in Rare Disease

Retricted access

Research article

First published 2015-11

Synergistic Efficacy from Gene Therapy with Coreceptor Blockade and a β 2 -Agonist in Murine Pompe Disease

Sang-oh Han, Songtao Li, Andrew Bird [...]

Human Gene Therapy

Open access

Review article

First published 2025

Lysosomal storage diseases in North America: a comprehensive review of enzyme therapies and unmet needs

Lunawati L. Bennett

Therapeutic Advances in Rare Disease

Retricted access

Research article

First published 2013-06

Phase I/II Trial of Adeno-Associated Virus–Mediated Alpha-Glucosidase Gene Therapy to the Diaphragm for Chronic Respiratory Failure in Pompe Disease: Initial Safety and Ventilatory Outcomes

Barbara K. Smith, Shelley W. Collins, Thomas J. Conlon [...]

Human Gene Therapy