Sage Journals: Discover world-class research

Open access

Case report

First published 2024-03-05

Repeated AAV9 Titer Determination in a Presymptomatic SMA Patient with Three SMN2 Gene Copies – A Case Report

Astrid Eisenkölbl, Manuel Pühringer

Journal of Neuromuscular Diseases

Retricted access

Research article

First published 2022-09

Prevalence of Anti-Adeno-Associated Virus Serotype 9 Antibodies in Adult Patients with Spinal Muscular Atrophy

Benjamin Stolte, Olivia Schreiber-Katz, René Günther [...]

Human Gene Therapy

Retricted access

Research article

First published 2023-05

Seroprevalence of Adeno-Associated Virus Neutralizing Antibodies in Males with Duchenne Muscular Dystrophy

Sumit Verma, Stella N. Nwosu, Raj Razdan [...]

Human Gene Therapy

Retricted access

Research article

First published 2026-2

Preclinical Assessment of Antibody Responses to Adeno-Associated Virus (AAV) Vector-Based Capsids of AAV2,AAV5,AAV8,or AAV9 in Laboratory Cynomolgus Macaques ( Macaca fascicularis ) of Asian or Mauritian Origin

Betina Pajaziti, Ulf Michgehl, Dragica Blazevic [...]

Human Gene Therapy

Retricted access

Research article

First published 2012-04

Adeno-Associated Virus Serotype 9 Transduction in the Central Nervous System of Nonhuman Primates

Lluis Samaranch, Ernesto A. Salegio, Waldy San Sebastian [...]

Human Gene Therapy

Retricted access

Research article

First published 2025-04

Prevalence of Neutralizing Antibodies to AAV2 and AAV9 in Individuals with Niemann-Pick Disease,Type C1

Avani V. Mylvara, Cristin D. Davidson, Derek Alexander [...]

Human Gene Therapy

Retricted access

Research article

First published 2012-07

Intranasal Vaccination with AAV5 and 9 Vectors Against Human Papillomavirus Type 16 in Rhesus Macaques

Karen Nieto, Christiane Stahl-Hennig, Barbara Leuchs [...]

Human Gene Therapy

Retricted access

Research article

First published 2017-08

Gene Delivery of Activated Factor VII Using Alternative Adeno-Associated Virus Serotype Improves Hemostasis in Hemophiliac Mice with FVIII Inhibitors and Adeno-Associated Virus Neutralizing Antibodies

Junjiang Sun, Baolai Hua, Xiaojing Chen [...]

Human Gene Therapy

Retricted access

Research article

First published 2016-05

Neutralizing Antibodies Against Adeno-Associated Viral Capsids in Patients with mut Methylmalonic Acidemia

Elizabeth A. Harrington, Jennifer L. Sloan, Irini Manoli [...]

Human Gene Therapy

Retricted access

Research article

First published 2024-01

Prevalence of Adeno-Associated Virus-9-Neutralizing Antibody in Chinese Patients with Duchenne Muscular Dystrophy

Cuijie Wei, Dongliang Li, Meng Zhang [...]

Human Gene Therapy

Search results